We are singularly focused on developing new therapies for patients with devastating rare diseases. We are passionate about the scientific process and seek to be nimble in all areas of our business.

Our employees are central to our ability to achieve our goals of helping patients. We’re looking for people to join our team who are collaborative, compassionate, resilient, and passionate about what we do.

We are proud to be an Equal Opportunity and Affirmative Action employer and are committed to fostering a diverse workplace environment where people can apply their unique backgrounds, experiences and ideas.

If you thrive in an entrepreneurial environment where you can make a real difference in people’s lives, we encourage you to review our open positions.

While we do not have any positions open at this time, we always encourage people to connect with us.